Golodirsen (SRP-4053) is a phosphorodiamidate morpholino oligomer (PMO) that specifically targets exon 53 of dystrophin pre-mRNA. Golodirsen can be used for the research of Duchenne muscular dystrophy (DMD).In VitroGolodirsen specifically targets exon 53 of dystrophin pre-mRNA, resulting in its exclusion from the final mRNA product. Skipping of exon 53 results in restoration of the mRNA reading frame and leads to the production of a partially internally deleted dystrophin protein with intact C and N-terminal regions. MCE has not independently confirmed the accuracy of these methods. They are for reference only.Form:Solid.
Specifications and Purity: ≥92%
Molecular Weight: 8647.00
- UPC:
- 10161527
- Condition:
- New
- HazmatClass:
- No
- WeightUOM:
- LB
- MPN:
- G649004-1mg
- CAS:
- 1422959-91-8
- Product Size:
- 1mg
akash.verma@cenmed.com
(732) 447-1115





